Prix Galien

Referenties Evrysdi® 1. Bijsluiter Evrysdi (risdiplam). Geraadpleegd op 7 maart 2022. Beschikbaar via https://www.roche.nl/content/dam/rochexx/roche-nl/ pdf/Evrysdi_II03_18nov2021_Leaf.pdf 2. SmPC Evrysdi (risdiplam). Geraadpleegd op 7 maart 2022. Beschikbaar via https://www.roche.nl/content/dam/rochexx/roche-nl/ pdf/Evrysdi_II03_18nov2021_SmPC.pdf Referenties Idefirix 1. Amro A, et al. J Ren Care 2014;40:23-33. 2. Zazzeroni L, et al. Kidney Blood Press Res 2017;42:717-727. 3. Sinnakirouchenan R, et al. Adv Chronic Kidney Dis 2011;18:428-432. 4. Jordan SC, et al. N Engl J Med. 2017;377(5):442-453. 5. Lonze BE, et al. Ann Surg. 2018;268(3):488–496. 8. 6. ManookM, et al. Lancet. 2017;389(10070):727–734 7. Jordan SC, et al. Immunotherapy 2015;7:377-398. 8. Aubert O,et al. BMJ 2015;351:h3557. 9. SmPC Idefirix oktober 2021 10. Jordan SC, et al. Transplantation 2021;105:1808-1817. 11. Kjellman C, et al. Am J Transplant 2021;21:3907-3918. 12. Winstedt L, et al. PLoS One. 2015;10(7):e0132011. 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European journal of pharmaceutics and biopharmaceutics : official journal of Arbeitsgemeinschaft fur Pharmazeutische Verfahrenstechnik eV. 2011;78(1):1-9. 6 Orkin C, Arasteh K, Gorgolas Hernandez-MoraM, Pokrovsky V, Overton ET, Girard PM, et al. Long-Acting Cabotegravir and Rilpivirine after Oral Induction for hiv-1 Infection. N Engl J Med. 2020;382(12):1124-35. 7 Swindells S, Andrade-Villanueva JF, Richmond GJ, Rizzardini G, Baumgarten A, MasiaM, et al. Long-Acting Cabotegravir and Rilpivirine for Maintenance of HIV-1 Suppression. N Engl J Med. 2020;382(12):1112-23. 8 Overton ET, Richmond GJ, Rizzardini G, Jaeger H, Orrell C, Nagimova F. Long-acting cabotegravir and rilpivirine dosed every 2 months in adults with hiv-1 infection (ATLAS-2M), 48-week results: a randomised, multicentre, open-label, phase 3b, non-inferiority study. Lancet (London, England). 2020. Referenties Takzhyro 1. LumryWR. Overview of epidemiology, pathophysiology, and disease progression in hereditary angioedema. 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Hereditary angiodema: a current state-of-the-art review, VII: Canadian Hungarian 2007 International Consensus Algorithm for the Diagnosis, Therapy, andManagement of Hereditary Angioedema. Ann Allergy Asthma Immunol. 2008;100(1 Suppl 2):S30-40. 8. Agostoni A, Aygoren-Pursun E, Binkley KE, et al. Hereditary and acquired angioedema: problems and progress: proceedings of the third C1 esterase inhibitor deficiency workshop and beyond. J Allergy Clin Immunol. 2004;114(3 Suppl):S51-131. 9. CugnoM, Nussberger J, Cicardi M, Agostoni A. Bradykinin and the pathophysiology of angioedema. International Immunopharmacology. 2003;3(3):311-317. 34 | PRIX GALIEN NEDERLAND 2022

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